| 标题 |
Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial |
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期刊:The Lancet Haematology 作者:Andreas Glenthøj; Eduard J. van Beers; Hanny Al‐Samkari; Vip Viprakasit; Kevin H.M. Kuo; et al 出版日期:2022-08-18 |
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(2025-6-4)