| 标题 |
Modified lentiviral globin gene therapy for pediatric β0/β0 transfusion-dependent β-thalassemia: A single-center, single-arm pilot trial |
| 网址 | |
| DOI | |
| 其它 |
期刊:Cell Stem Cell 作者:Shiqi Li; Sikai Ling; Dawei Wang; Xiaoyuan Wang; Fangyuan Hao; et al 出版日期:2024-05-16 |
| 求助人 | |
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(2025-6-4)