| 标题 |
Gene-Corrected Human iPSC–Derived Cardiomyocytes and Skeletal Muscles Reveal Partial Dystrophin Dp427 Preservation and Cardiac Dp116 Expression in Duchenne Muscular Dystrophy Patient With a Splice-Site Mutation in Intron 68 (c.9975-1G>T) |
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| 其它 |
期刊:Circulation: Genomic and Precision Medicine 作者:Marta Białobrzeska; Marta Przymuszała; Paweł Ferdek; Iryna Viestia; Anna Potulska-Chromik; et al 出版日期:2026-09-25 |
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(2025-6-4)