亨廷顿病
疾病
临床试验
医学
生物信息学
生物
内科学
作者
Mena Farag,Sarah J. Tabrizi,Edward J. Wild
出处
期刊:Journal of Huntington's disease
[IOS Press]
日期:2024-10-26
卷期号:13 (4): 409-418
被引量:4
标识
DOI:10.1177/18796397241293955
摘要
In this edition of the Huntington's Disease Clinical Trials Update, we expand on the ongoing extension study of PTC518 from PTC Therapeutics, including 12-month interim results from the parent study. We also discuss 24-month interim results from uniQure's AMT-130 program and 28-week follow-up results from Wave Life Sciences' SELECT-HD clinical trial of WVE-003. Additionally, we provide a comprehensive listing of all currently registered and ongoing clinical trials in Huntington's disease.
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