| 标题 |
Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial |
| 网址 | |
| DOI | |
| 其它 |
期刊:Lancet Neurology 作者:Benedikt Schoser; Mark Roberts; Barry J. Byrne; Sheela Sitaraman; Hai Jiang; et al 出版日期:2021-11-17 |
| 求助人 | |
| 下载 | 求助已完成,仅限求助人下载。 |
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(2025-6-4)