形状记忆合金*
脊髓性肌萎缩
医学
疾病
临床试验
神经科学
物理医学与康复
萎缩
生物信息学
病理
数学
组合数学
生物
作者
Gamze Bora,Ayşe Yeşbek-Kaymaz,Can Ebru Bekircan-Kurt,VİLDAN GÖKNUR HALİLOĞLU,Haluk Topaloğlu,Hayat Erdem‐Yurter,Sevim Erdem‐Özdamar
摘要
Proximal spinal muscular atrophy (SMA) is an inherited neurodegenerative disease with a heterogeneous clinical phenotype. Although there is no cure for SMA, several strategies are currently being developed. In this review, we summarize the ongoing clinical trials and molecular mechanisms of successful approaches to SMA treatment.
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