| 标题 |
Safety of AAV gene therapy programs for neurological indications – Learning from programs in non-lysosomal disorders |
| 网址 | |
| DOI | |
| 其它 |
February 2026,Molecular Genetics and Metabolism 147(2):109393 https://www.sciencedirect.com/science/article/pii/S1096719225003853?via%3Dihub https://www.researchgate.net/publication/400437675_Safety_of_AAV_gene_therapy_programs_for_neurological_indications_-_Learning_from_programs_in_non-lysosomal_disorders |
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(2025-6-4)